You have 9 free searches left this month | for more free features.
Clincosm LogoSign in Get a demo

AAV Vector

Showing 1 - 25 of 756
STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS
LAST UPDATED

Hemophilia A Trial in Tianjin (Single dose intravenous injection of BBM 002)

Not yet recruiting
  • Hemophilia A
  • Single dose intravenous injection of BBM 002
  • Tianjin, Tianjin, China
    Institute of Hematology & Blood Diseases Hospital
Jul 7, 2022

Hemophilia A, Gene Therapy Trial in Tianjin (Injection of GS001)

Recruiting
  • Hemophilia A
  • Gene Therapy
  • Injection of GS001
  • Tianjin, Tianjin, China
    Chinese Academy of Medical Science and Blood Disease Hospital
Sep 19, 2022

Hemophilia B Trial in Tianjin (Single dose intravenous injection of BBM-H901)

Active, not recruiting
  • Hemophilia B
  • Single dose intravenous injection of BBM-H901
  • Tianjin, Tianjin, China
    Institute of Hematology & Blood Diseases Hospital
Dec 12, 2021

Study Medicines Called Giroctocogene Fitelparvovec and

Recruiting
  • Hemophilia A
  • Hemophilia B
  • Testing of hepatic AAV Vector integration
  • Madison, Mississippi
    Mississippi Center For Advanced Medicine
Dec 1, 2022

Lysosomal Diseases, Gangliosidosis, GM1 Trial run by the NHGRI (biological, drug, diagnostic test, other, procedure, behavioral)

Recruiting
  • Lysosomal Diseases
  • +2 more
  • AAV9-GLB1
  • +20 more
  • Bethesda, Maryland
    National Institutes of Health Clinical Center
Jan 19, 2023

Achromatopsia Trial in Ann Arbor, London (adeno-associated virus vector AAV- CNGA3)

Completed
Has Results
  • Achromatopsia
  • adeno-associated virus vector AAV- CNGA3
  • Ann Arbor, Michigan
  • +1 more
Feb 10, 2022

Hemophilia A, Gene Therapy, Clotting Disorders Trial in Johannesburg, London, Southampton (Valoctocogene Roxaparvovec)

Recruiting
  • Hemophilia A
  • +3 more
  • Valoctocogene Roxaparvovec
  • Seoul, Korea, Republic of
  • +8 more
Jan 6, 2023

Study of AAV5-hFIX in Severe or Moderately Severe Haemophilia B

Active, not recruiting
  • Hemophilia B
  • AAV5-hFIX
  • Berlin, Germany
  • +5 more
Jan 17, 2023

Long Term Follow-Up Gene Therapy Study for XLRP RPGR

Recruiting
  • X-Linked Retinitis Pigmentosa
  • AAV-RPGR
  • Boston, Massachusetts
  • +3 more
Dec 5, 2022

Squamous Cell Head Neck Cancer, Radiation Induced Xerostomia, Salivary Hypofunction Trial run by the (AAV2hAQP1)

Recruiting
  • Squamous Cell Head and Neck Cancer
  • +2 more
  • AAV2hAQP1
  • Bethesda, Maryland
    National Institutes of Health Clinical Center, 9000 Rockville Pi
May 3, 2022

Hemophilia B Trial in Denmark, Germany, Netherlands (AAV5-hFIX)

Completed
Has Results
  • Hemophilia B
  • AAV5-hFIX
  • Copenhagen, Denmark
  • +6 more
Jun 1, 2022

LCA5 Trial (AAV8.hLCA5)

Not yet recruiting
  • LCA5
  • AAV8.hLCA5
  • (no location specified)
Nov 22, 2022

Hemophilia B Trial in United States (AAV5-hFIXco-Padua (AMT-061))

Active, not recruiting
Has Results
  • Hemophilia B
  • AAV5-hFIXco-Padua (AMT-061)
  • Los Angeles, California
  • +3 more
May 17, 2022

Achromatopsia Trial in Ann Arbor, London (either AAV - CNGB3 or AAV - CNGA3)

Active, not recruiting
  • Achromatopsia
  • either AAV - CNGB3 or AAV - CNGA3
  • Ann Arbor, Michigan
  • +1 more
Jan 13, 2022

Canavan Disease Trial in Boston (AAV9 BBP-812)

Recruiting
  • Canavan Disease
  • AAV9 BBP-812
  • Boston, Massachusetts
    Massachusetts General Hospital (MGH); Center for Rare Neurologic
Mar 12, 2022

Hereditary Angioedema, HAE Trial in United States (Dose 1 of BMN 331, Dose 2 of BMN 331, Dose 3 of BMN 331)

Recruiting
  • Hereditary Angioedema
  • HAE
  • Dose 1 of BMN 331
  • +4 more
  • Birmingham, Alabama
  • +11 more
Jan 26, 2023

Danon Disease Trial in La Jolla, Philadelphia (RP-A501)

Recruiting
  • Danon Disease
  • RP-A501
  • La Jolla, California
  • +1 more
Oct 17, 2023

Friedreich Ataxia, Cardiomyopathies, Cardiac Hypertrophy Trial in New York (AAVrh.10hFXN, serotype rh.10 adeno-associated virus

Recruiting
  • Friedreich Ataxia
  • +3 more
  • AAVrh.10hFXN, serotype rh.10 adeno-associated virus (AAV) gene transfer vector expressing the cDNA coding for human FXN
  • Prednisone
  • New York, New York
    Weill Cornell Medicine
Jul 15, 2022

Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)

Active, not recruiting
  • Inherited Retinal Dystrophy Due to RPE65 Mutations
  • AAV2-hRPE65v2
  • (no location specified)
Dec 9, 2021

Inherited Retinal Dystrophy Due to RPE65 Mutations, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia

Active, not recruiting
Has Results
  • Inherited Retinal Dystrophy Due to RPE65 Mutations
  • Leber Congenital Amaurosis
  • AAV2-hRPE65v2,voretigene neparvovec-rzyl
  • Iowa City, Iowa
  • +1 more
Dec 9, 2021

Choroideremia Trial in Edmonton (rAAV2.REP1 vector)

Completed
  • Choroideremia
  • rAAV2.REP1 vector
  • Edmonton, Alberta, Canada
    University of Alberta
May 16, 2022

Coronavirus Infection, COVID-19 Trial in Saint Petersburg (Low dose BCD-250 injection, High dose BCD-250 injection, Low dose or

Recruiting
  • Coronavirus Infection
  • COVID-19
  • Low dose BCD-250 injection
  • +3 more
  • Saint Petersburg, Russian Federation
  • +1 more
Sep 7, 2021

Crigler-Najjar Syndrome Trial in France, Italy, Netherlands (GNT0003)

Recruiting
  • Crigler-Najjar Syndrome
  • GNT0003
  • Clamart, France
  • +3 more
Jun 1, 2021

Congenital Adrenal Hyperplasia Trial in United States (AAV BBP-631)

Recruiting
  • Congenital Adrenal Hyperplasia
  • AAV BBP-631
  • Los Angeles, California
  • +6 more
Jul 29, 2022

Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Trial in Taipei (gene therapy)

Active, not recruiting
  • Aromatic L-amino Acid Decarboxylase (AADC) Deficiency
  • gene therapy
  • Taipei, Taiwan
    National Taiwan University Hospital
Aug 4, 2021